CFDB - Cystic Fibrosis DataBase

primary studies published RCT

Comparative efficacy and safety of 4 randomized regimens to treat early Pseudomonas aeruginosa infection in children with cystic fibrosis.

Study design (if review, criteria of inclusion for studies)

Randomized controlled trial. Multicenter trial in the United States. Intention-to-treat analysis

Participants

304 children with cystic fibrosis aged 1 to 12 years within 6 months of P aeruginosa detection.

Interventions

Participants were randomized to 1 of 4 antibiotic regimens for 18 months (six 12-week quarters) between December 2004 and June 2009. Participants randomized to cycled therapy received tobramycin inhalation solution (300 mg twice a day) for 28 days, with oral ciprofloxacin (15-20 mg/kg twice a day) or oral placebo for 14 days every quarter, while participants randomized to culture-based therapy received the same treatments only during quarters with positive P aeruginosa cultures.

Outcome measures

exacerbation rates, P aeruginosa- positive culture. Adverse events

Main results

There was no interaction between treatments. There were no statistically significant differences in exacerbation rates between cycled and culture-based groups (hazard ratio, 0.95; 95% confidence interval [CI], 0.54-1.66) or ciprofloxacin and placebo (hazard ratio, 1.45; 95% CI, 0.82-2.54). The odds ratios of P aeruginosa- positive culture comparing the cycled vs culture-based group were 0.78 (95% CI, 0.49-1.23) and 1.10 (95% CI, 0.71-1.71) comparing ciprofloxacin vs placebo. Adverse events were similar across groups.

Authors' conclusions

No difference in the rate of exacerbation or prevalence of P aeruginosa positivity was detected between cycled and culture-based therapies. Adding ciprofloxacin produced no benefits.

Keywords: child; Anti-Bacterial Agents; Bacterial Infections; Infection; Pseudomonas aeruginosa; Pseudomonas; Respiratory Tract Diseases; Respiratory Tract Infections; tobramycin; ciprofloxacin; pharmacological_intervention; Oral; Inhalation OR nebulised; Quinolones; Aminoglycosides;