Tezacaftor-Ivacaftor in Residual-Function Heterozygotes with Cystic Fibrosis.
primary studies published RCT
Details- 2017
- Rowe SM
Lumacaftor/Ivacaftor Treatment of Patients with Cystic Fibrosis Heterozygous for F508del-CFTR.
primary studies published RCT
Details- 2017
- Rowe SM
Tezacaftor-Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508del.
primary studies published RCT
Details- 2017
- Taylor-Cousar JL
Long-Term Pulmonal Therapy of Cystic Fibrosis-Patients with Amitriptyline.
primary studies published RCT
Details- 2016
- Adams C
A randomized controlled trial to evaluate the lung clearance index as an outcome measure for early phase studies in patients with cystic fibrosis.
primary studies published RCT
Details- 2016
- Amin R
Nutritional Status Improved in Cystic Fibrosis Patients with the G551D Mutation After Treatment with Ivacaftor.
primary studies published RCT
Details- 2016
- Borowitz D
Pilot Randomized Controlled Trial Evaluating the Effect of Hypertonic Saline With and Without Hyaluronic Acid in Reducing Inflammation in Cystic Fibrosis.
primary studies published RCT
Details- 2016
- Brivio A
Infant lung function tests as endpoints in the ISIS multicenter clinical trial in cystic fibrosis.
primary studies published RCT
Details- 2016
- Davis SD
A randomised trial of hypertonic saline during hospitalisation for exacerbation of cystic fibrosis.
primary studies published RCT
Details- 2016
- Dentice RL
Efficacy and safety of lumacaftor/ivacaftor combination therapy in patients with cystic fibrosis homozygous for Phe508del CFTR by pulmonary function subgroup: a pooled analysis.
primary studies published RCT
Details- 2016
- Elborn JS