CFDB - Cystic Fibrosis DataBase

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Chest computed tomography outcomes in a randomized clinical trial in cystic fibrosis: Lessons learned from the first ataluren phase 3 study.

primary studies  published RCT

Details
  • 2020
  • Tiddens HAWM

Intravenous versus oral antibiotics for eradication of Pseudomonas aeruginosa in cystic fibrosis (TORPEDO-CF): a randomised controlled trial.

primary studies  published RCT

Details
  • 2020
  • Hewer SCL

Long-term docosahexaenoic acid (DHA) supplementation in cystic fibrosis patients: a randomized, multi-center, double-blind, placebo-controlled trial.

primary studies  published RCT

Details
  • 2020
  • López-Neyra A

A four week trial of hypertonic saline in children with mild cystic fibrosis lung disease: Effect on mucociliary clearance and clinical outcomes.

primary studies  published RCT

Details
  • 2020
  • Donaldson SH

Aerosolized lancovutide in adolescents (≥12 years) and adults with cystic fibrosis - a randomized trial.

primary studies  published RCT

Details
  • 2020
  • Eber E

Improved residual fat malabsorption and growth in children with cystic fibrosis treated with a novel oral structured lipid supplement: A randomized controlled trial.

primary studies  published RCT

Details
  • 2020
  • Stallings VA

Correction: Improved residual fat malabsorption and growth in children with cystic fibrosis treated with a novel oral structured lipid supplement: A randomized controlled trial.

primary studies  published RCT

Details
  • 2020
  • Stallings VA

Effects of low glycemic index/high-fat, high-calorie diet on glycemic control and lipid profiles of children and adolescence with cystic fibrosis: A randomized double-blind controlled clinical trial.

primary studies  published RCT

Details
  • 2020
  • Gorji Z

Effects of synbiotic supplementation on the pulmonary manifestations and anthropometric measurements in children with cystic fibrosis- a randomized clinical trial

primary studies  published RCT

Details
  • 2020
  • N Bilan, E Marefat, M Nouri-Vaskeh, L Nikniaz, Z Nikniaz

Efficacy and safety of ataluren in patients with nonsense-mutation cystic fibrosis not receiving chronic inhaled aminoglycosides: The international, randomized, double-blind, placebo-controlled Ataluren Confirmatory Trial in Cystic Fibrosis (ACT CF).

primary studies  published RCT

Details
  • 2020
  • Konstan MW