CFDB - Cystic Fibrosis DataBase

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A randomised controlled trial of rosuvastatin for the prevention of aminoglycoside-induced kidney toxicity in children with cystic fibrosis.

primary studies  published RCT

Details
  • 2020
  • McWilliam SJ

CFTR activity is enhanced by the novel corrector GLPG2222, given with and without ivacaftor in two randomized trials.

primary studies  published RCT

Details
  • 2019
  • Bell SC

Non-invasive ventilation versus oxygen therapy in cystic fibrosis: A 12-month randomized trial.

primary studies  published RCT

Details
  • 2019
  • Milross MA

Lumacaftor/Ivacaftor reduces pulmonary exacerbations in patients irrespective of initial changes in FEV1.

primary studies  published RCT

Details
  • 2019
  • McColley SA

Impact of hypertonic saline nebulisation combined with oscillatory positive expiratory pressure on sputum expectoration and related symptoms in cystic fibrosis: a randomised crossover trial.

primary studies  published RCT

Details
  • 2019
  • San Miguel-Pagola M

Exenatide corrects postprandial hyperglycaemia in young people with cystic fibrosis and impaired glucose tolerance: A randomized crossover trial.

primary studies  published RCT

Details
  • 2019
  • Geyer MC

Dornase alfa during lower respiratory tract infection post-lung transplantation: a randomized controlled trial.

primary studies  published RCT

Details
  • 2019
  • Tarrant BJ

Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial.

primary studies  published RCT

Details
  • 2019
  • Heijerman HGM

Sildenafil improves exercise capacity in patients with cystic fibrosis: a proof-of-concept clinical trial.

primary studies  published RCT

Details
  • 2019
  • Rodriguez-Miguelez P

Elexacaftor-Tezacaftor-Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele.

primary studies  published RCT

Details
  • 2019
  • Middleton PG