CFDB - Cystic Fibrosis DataBase

Emulated trial investigating effects of multiple treatments: estimating combined effects of mucoactive nebulisers in cystic fibrosis using registry data.

primary studies  published, non RCT

Details
  • 2023
  • Granger E

Impact of lumacaftor/ivacaftor and tezacaftor/ivacaftor on treatment response in pulmonary exacerbations of F508del/F508del cystic fibrosis.

primary studies  published, non RCT

Details
  • 2023
  • McElvaney OJ

Heterogeneous liver on research ultrasound identifies children with cystic fibrosis at high risk of advanced liver disease.

primary studies  published, non RCT

Details
  • 2023
  • Siegel MJ

Newborn screening alone insufficient to improve pulmonary outcomes for cystic fibrosis.

primary studies  published, non RCT

Details
  • 2021
  • Barreda CB

Challenged Urine Bicarbonate Excretion as a Measure of Cystic Fibrosis Transmembrane Conductance Regulator Function in Cystic Fibrosis.

primary studies  published, non RCT

Details
  • 2022
  • Berg P

The long-term effects of insulin use in incident cystic fibrosis-related diabetes: a target trial emulated using longitudinal national registry data.

primary studies  published, non RCT

Details
  • 2022
  • Granger E

Feasibility and acceptability of a CF-specific cognitive-behavioral preventive intervention for adults integrated into team-based care.

primary studies  published, non RCT

Details
  • 2022
  • Friedman D

Health care costs in a randomized trial of antimicrobial duration among cystic fibrosis patients with pulmonary exacerbations.

primary studies  published, non RCT

Details
  • 2022
  • Gold LS

Impact of pharmacy services on time to elexacaftor-tezacaftor-ivacaftor initiation.

primary studies  published, non RCT

Details
  • 2022
  • Roder L

Feasibility and efficacy of combined pancreatic islet-lung transplantation in cystic fibrosis related diabetes -PIM study: a multicenter phase 1-2 trial.

primary studies  published, non RCT

Details
  • 2022
  • Rakotoarisoa L