Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial.
primary studies published RCT
Details- 2019
- Heijerman HGM
Sildenafil improves exercise capacity in patients with cystic fibrosis: a proof-of-concept clinical trial.
primary studies published RCT
Details- 2019
- Rodriguez-Miguelez P
Elexacaftor-Tezacaftor-Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele.
primary studies published RCT
Details- 2019
- Middleton PG
Airway clearance physiotherapy improves ventilatory dynamics during exercise in patients with cystic fibrosis: a pilot study.
primary studies published RCT
Details- 2019
- Vendrusculo FM
A smartphone application for reporting symptoms in adults with cystic fibrosis improves the detection of exacerbations: Results of a randomised controlled trial.
primary studies published RCT
Details- 2019
- Wood J
Inhaled hypertonic saline in preschool children with cystic fibrosis (SHIP): a multicentre, randomised, double-blind, placebo-controlled trial.
primary studies published RCT
Details- 2019
- Ratjen F
Effects of Exercise Intervention Program on Bone Mineral Accretion in Children and Adolescents with Cystic Fibrosis: A Randomized Controlled Trial.
primary studies published RCT
Details- 2019
- Gupta S
Clustered randomized controlled trial of a clinic-based problem-solving intervention to improve adherence in adolescents with cystic fibrosis.
primary studies published RCT
Details- 2019
- Quittner AL
Vitamin D for the Immune System in Cystic Fibrosis (DISC): a double-blind, multicenter, randomized, placebo-controlled clinical trial.
primary studies published RCT
Details- 2019
- Tangpricha V
Supporting medication adherence for adults with cystic fibrosis: a randomised feasibility study.
primary studies published RCT
Details- 2019
- Hind D