CFDB - Cystic Fibrosis DataBase

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Infant lung function tests as endpoints in the ISIS multicenter clinical trial in cystic fibrosis.

primary studies  published RCT

Details
  • 2016
  • Davis SD

A randomised trial of hypertonic saline during hospitalisation for exacerbation of cystic fibrosis.

primary studies  published RCT

Details
  • 2016
  • Dentice RL

Efficacy and safety of lumacaftor/ivacaftor combination therapy in patients with cystic fibrosis homozygous for Phe508del CFTR by pulmonary function subgroup: a pooled analysis.

primary studies  published RCT

Details
  • 2016
  • Elborn JS

A phase 3, multi-center, multinational, randomized, double-blind, placebo-controlled study to evaluate the efficacy and safety of levofloxacin inhalation solution (APT-1026) in stable cystic fibrosis patients.

primary studies  published RCT

Details
  • 2016
  • Flume PA

Continuous alternating inhaled antibiotics for chronic pseudomonal infection in cystic fibrosis.

primary studies  published RCT

Details
  • 2016
  • Flume PA

Inhaled alpha1-proteinase inhibitor therapy in patients with cystic fibrosis.

primary studies  published RCT

Details
  • 2016
  • Gaggar A

A Prospective, Randomized, Double-Blind, Parallel-Group, Comparative Effectiveness Clinical Trial Comparing a Powder Vehicle Compound of Vitamin D With an Oil Vehicle Compound in Adults With Cystic Fibrosis.

primary studies  published RCT

Details
  • 2016
  • Hermes WA

Safety and Efficacy of a Novel Microbial Lipase in Patients with Exocrine Pancreatic Insufficiency due to Cystic Fibrosis: A Randomized Controlled Clinical Trial.

primary studies  published RCT

Details
  • 2016
  • Heubi JE

Assessment of safety and efficacy of long-term treatment with combination lumacaftor and ivacaftor therapy in patients with cystic fibrosis homozygous for the F508del-CFTR mutation (PROGRESS): a phase 3, extension study.

primary studies  published RCT

Details
  • 2016
  • Konstan MW

One-year safety and efficacy of tobramycin powder for inhalation in patients with cystic fibrosis.

primary studies  published RCT

Details
  • 2016
  • Konstan MW